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A Multimodal Screening Platform for Endogenous Dipeptide Repeat Proteins in C9orf72 Patient Ipsc Neurons

Benedikt V Hölbling, Yashica Gupta, Paolo M Marchi, Magda L Atilano,Michael Flower,Enric Ureña, Rajkumar A Goulden, Hannah K Dobbs,Eszter Katona, Alla Mikheenko, Ashling Giblin, Ali Raza Awan, Chloe L Fisher-Ward, Niamh O'Brien, Deniz Vaizoglu, Liam Kempthorne, Katherine M Wilson,Lauren M Gittings, Mireia Carcolé, Marc-David Ruepp,Sarah Mizielinska, Linda Partridge,Pietro Fratta, Sarah J Tabrizi,Bhuvaneish T Selvaraj,Siddharthan Chandran, Emma Armstrong, Paul Whiting, Adrian M Isaacs

Cell reports(2025)

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CP: Neuroscience
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