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Generation of C9orf72 Repeat Knock-in Ipsc Lines for Modelling ALS and FTD

Rachel Coneys, Alexander J Cammack, Remya Raghavan-Nair,David Thompson,Jonas Mechtersheimer,Mireia Carcolé, Yashica Gupta, Gabriel E Rech,Michael Flower,Niamh O'Brien,Marc-David Ruepp,Sarah Mizielinska, Fiona Ducotterd,Sarah J Tabrizi,Elizabeth M.C Fisher, Tom J Cunningham,Michael Ward, Bill Skarnes,Adrian Isaacs

biorxiv(2025)

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