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Independent Genetic Strategies Define the Scope and Limits of CDKL5 Deficiency Disorder Reversal

Xie Song, Zijie Xia, Dayne Martinez,Bing Xu, Zachary Spritzer, Yanjie Zhang, Erin Nugent,Yugong Ho,Barbara Terzic,Zhaolan Zhou

Cell Reports Medicine(2025)

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关键词
CDKL5 deficiency disorder,CDD,genetic reversal,behavioral phenotype,learning and memory,epilepsy,mouse model,clinical trial design
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