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High-efficiency Base Editing in the Retina in Primates and Human Tissues

Alissa Muller,Jack Sullivan,Wibke Schwarzer,Mantian Wang,Cindy Park-Windhol,Pascal W. Hasler, Lucas Janeschitz-Kriegl, Mert Duman, Beryll Klingler, Jane Matsell, Simon Manuel Hostettler, Patricia Galliker, Yanyan Hou, Pierre Balmer, Tamás Virág,Luis Alberto Barrera,Lauren Young,Quan Xu, Dániel Péter Magda,Ferenc Kilin, Arogya Khadka,Pierre-Henri Moreau,Lyne Fellmann,Thierry Azoulay, Mathieu Quinodoz, Duygu Karademir, Juna Leppert, Alex Fratzl,Georg Kosche,Ruchi Sharma,Jair Montford, Marco Cattaneo, Mikaël Croyal, Therese Cronin,Simone Picelli,Alice Grison,Cameron S. Cowan,Ákos Kusnyerik,Philipp Anders, Magdalena Renner,Zoltán Zsolt Nagy,Arnold Szabó,Kapil Bharti,Carlo Rivolta, Hendrik P. N. Scholl,David Bryson,Giuseppe Ciaramella,Botond Roska,Bence György

Nature Medicine(2025)

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