REMEDY Corrects Heterozygous Mutations Independent of Exogenous Donor Template with High Efficiency
Yasemin Sezgin,Noushin Saljoughian, Genesis Snyder,Colin Maguire,Ebru Erzurumluoglu Gokalp, Eleonora D'Ambrosio,Devi Jaganathan,Burcak Ozes,Zarife Sahenk,Sriram Vaidyanathan,Jerry R. Mendell,Nizar Y. Saad,Roshini S. Abraham,Juhi Bagaitkar,Susan D. Reynolds,Allison M. Bradbury,Meisam Naeimi Kararoudi MOLECULAR THERAPY(2024)
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