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LARGE DELETIONS IN THE F8 GENE PREDICT IMMUNE TOLERANCE INDUCTION FAILURE IN PEOPLE WITH SEVERE HEMOPHILIA A

I Oomen,A Abdi, L Broer,RM Camelo, FMRA Callado,LEM Carvalho, IL Calcaterra,M Carcao,G Castaman,JCJ Eikenboom,K Fischer,VKB Franco,J Geissler, TW Kuijpers, FWG Leebeek,D Lillicrap,CS Lorenzato, ME Mancuso,D Matino, MND Di Minno

Hematology, Transfusion and Cell Therapy(2024)

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