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271 Prime Editing Functionally Corrects Rare and Common Cystic Fibrosis–causing Mutations in Patient-Derived Organoids and Airway Epithelia

M. Bulcaen, P. Kortleven, R. Liu,G. Maule,E. Dreano, M. Kelly,M. Ensinck, S. Thierie, M. Smits,M. Ciciani,A. Hatton, B. Chevalier,A.S. Ramalho, X. Casadevall i Solvas,Z. Debyser,F. Vermeulen,R. Gijsbers,I. Sermet-Gaudelus,A. Cereseto,M. Carlon

Journal of Cystic Fibrosis(2024)

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