CRISPR Base Editing to Create Potential Charcot–Marie–Tooth Disease Models with High Editing Efficiency: Human Induced Pluripotent Stem Cell Harboring SH3TC2 Variants
Biomedicines(2024)
关键词
hiPSCs,CRISPR-Cas9,disease cellular model,Charcot-Marie-Tooth (CMT),SH3TC2,HEK293-T
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