Genome-edited hematopoietic stem cells as a curative approach for Gaucher disease type 1 Luisa N. Pimentel Vera, Marc Gastou, Jessica Arozqueta-Basurto,Pasqualina Colella,Allan Feng,Edina Poletto,Natalia Gomez-OspinaMOLECULAR GENETICS AND METABOLISM(2024)引用 0|浏览1暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要