Effect Size Analysis of Cipaglucosidase Alfa Plus Miglustat Versus Alglucosidase Alfa in ERT-experienced Adults with Late-onset Pompe Disease in PROPEL (S21.003)Hani Kushlaf,Drago Bratkovic,Barry Byrne,Kristl Claeys,Jordi Diaz-Manera,Mazen Dimachkie,Priya Kishnani,Mark Roberts,Antonio Toscano, Jeff Castelli, Frederick Holdbrook, Sheela Das,Yasmine Wasfi,Benedikt Schoser,Tahseen MozaffarNeurology(2024)引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要