ACADVL−/−/ACADL−/− mice demonstrate symptoms of very long chain acyl-CoA dehydrogenase deficiency that are rescued by AAV9 gene therapy

Jerry Vockley,Xue-Jun Zhao,Bianca Seminotti,Shakuntala Basu, Clinton Van't Land, Michele Stone,Jason Mallory, Pilar Prentiss, Sarah Jaslow, Alex Turner, Lakmini Wasala,Al-Walid Mohsen

Molecular Genetics and Metabolism(2024)

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