Pegtibatinase, an investigational enzyme replacement therapy, for the treatment of classical homocystinuria (HCU): Design of the harmony Phase 3 studyJanet Thomas,Tawfeg Ben-Omran, Harvey Levy,Francois Maillot, Sharon McDermott, Sergio Slawka,Can FiciciogluMolecular Genetics and Metabolism（2024）引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
