Engineered CardiacSpecific AAV Capsids From a Novel Next-Generation Platform (next-CAP) With Cross-Species Selection for Cardiac-Targeted Gene Therapy

Jorg Schweiggert,Gregor Habeck,Rabea Hinkel,Dorothea Kehr, Kristin Cimen, Xenia Kramp, Marc Lerchenmueller,Hugo Katus,Patrick Most, Martin Busch

CIRCULATION(2023)

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关键词
Gene therapy.,Gene transfer.,Heart Failure.,Viruses
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