Genome integrity and scalable gmp-compliant manufacturing of hdr gene edited cd4+t cells for the treatment of hyper igm 1

D. Canarutto, C. Asperti, V. Vavassori, S. Porcellini, E. Rovelli, M. Paulis, S. Ferrari, T. Plati,L. Sergi Sergi, A. Villa, M. Radrizzani, L. Naldini

HUMAN GENE THERAPY(2023)

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