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Small-Molecule-Directed Endogenous Regeneration of Visual Function in a Mammalian Retinal Degeneration Model

Daphna Mokady,Jason Charish, Patrick Barretto-Burns,Kenneth N. Grise,Brenda L. K. Coles, Susanne Raab,Arturo Ortin-Martinez, Alex Muller,Bernhard Fasching, Payal Jain, Micha Drukker,Derek van der Kooy,Matthias Steger

INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES(2024)

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关键词
small molecule,regenerative medicine,inherited retinal diseases,retina,photoreceptors,functional recovery
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