Long-term follow-up of onasemnogene abeparvovec gene therapy in patients with spinal muscular atrophy (SMA) type 1

J. Mendell, M. Wigderson, I. Alecu,L. Yang, L. Mehl,A. Connolly

NEUROMUSCULAR DISORDERS(2023)

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spinal muscular atrophy,abeparvovec onasemnogene therapy,onasemnogene therapy,long-term
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