Comparison of Cardiac Specific Promoters to Liver-Specific miRNA Targets to Maximize Cardiac vs Liver Expression Following Intravenous AAVrh.10-Mediated Cardiac Gene Therapy

Abhishek Bose,Neil R. Hackett, Nadir Khan-Yusufzai,Katie M. Stiles,Ronald G. Crystal

MOLECULAR THERAPY(2023)

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