Delivery of PMP22-Targeting shRNA by ARMMs as a Disease-Modifying Therapeutic Approach for Charcot Marie Tooth 1A

Nedyalka Valkov, Shu-Lin Liu,Chris Chatzinakos, Bhavesh Gurwani, Qiyu Wang,Lucy Sun, Kristin Luther, Adam Francoeur, Leah Gens, Alysia Bryant,Joseph F. Nabhan

MOLECULAR THERAPY(2023)

引用 0|浏览0
暂无评分
AI 理解论文
溯源树
样例
生成溯源树,研究论文发展脉络
Chat Paper
正在生成论文摘要