Development of a Self-Complementary AAV.U7snRNA Vector for Efficient Dystrophin Exon 53 SkippingRandolph Qian,Steven J. Foltz, Lan Jin, Ting Chen,Chunping Qiao,Kirk W. Elliott, Ikram Hafiz,Jason Yang,Subha Karumuthil-Melethil,Joseph T. Bruder,Olivier F. Danos,Ye LiuMOLECULAR THERAPY(2023)引用 0|浏览2暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要