Preclinical Development of an Ex Vivo Gene Therapy for Mucopolysaccharidosis Type IIValentina Poletti,Sabyasachi Das,Fatlum Rruga, Agnese Dimartino,Annita Montepeloso,Janki Patel,Francesca Ferro,Eleonora Cavalca,Letterio Politi,Alessandra BiffiMOLECULAR THERAPY(2023)引用 0|浏览10暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要