Massive Diversity Capsid Screening and Machine Learning Identify Next-Generation AAV for Targeted Tissue Biodistribution

Thomas A. Packard,Kevin C. Stein, Erica A. Cates,Jeremy E. Bazinet, W. Daisy Han,Yue Jiang, Maria F. Andrade, Thomas J. Long, David J. Huss,Ronald J. Hause,Adrian W. Briggs

MOLECULAR THERAPY(2023)

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