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In Vivo Silencing of Regulatory Elements Using a Single AAV-CRISPRi Vector

P. Laurette, C. Cao,D. Ramanujam,M. Schwaderer, T. Lueneburg, S. Kuss, L. Weiss, R. Dilshat, E. E. M. Furlong,F. Rezende,S. Engelhardt,R. Gilsbach

Circulation Research(2024)

Cited 1|Views13
Key words
epigenetic repression,gene editing,gene silencing,genetic therapy,genomics
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