Lentiviral-Mediated Gene Therapy for Fanconi Anemia [Group A]: Results from Global RP-L102 Clinical Trials
Agnieszka Czechowicz,Julian Sevilla,Claire Booth,Susana Navarro,Rajni Agarwal,Josune Zubicaray,Paula Rio,Kritika Chetty, Grainne O'Toole,Jinhua Xu-Bayford,Philip Ancliff,Elena Sebastian,Grace Choi,Miriam Zeini,Eileen Nicoletti,Cindy Eide,John E. Wagner,Gayatri Rao,Adrian J. Thrasher,Jonathan Schwartz,Maria-Grazia Roncarolo,Juan A. Bueren PEDIATRIC BLOOD & CANCER(2023)
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