Efficacy and safety of odevixibat in patients with alagille syndrome: top-line results from assert, a phase 3, double-blind, randomized, placebo-controlled studyNadia Ovchinsky,Madeleine Aumar,Alastair Baker,Ulrich Baumann,Philip Bufler,Mara Cananzi,Piotr Czubkowski,Ozlem Durmaz,Ryan Fischer,Giuseppe Indolfi,Wikrom Karnsakul, Florence Lacaille Way S. Lee,Giuseppe Maggiore,Philip Rosenthal,Mathias Ruiz,Etienne Sokal,Ekkehard Sturm,Wendy Van der Woerd,Henkjan J. Verkade, Andrew Wehrman, Christine Clemson,Qifeng Yu,Quanhong Ni, Jessica Ruvido, Susan Manganaro,Jan P. MattssonHEPATOLOGY(2023)引用 0|浏览18暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要