Update on phase 1/2 clinical trials for MPS I and MPS II using ZFN-mediated in vivo genome editingPaul Harmatz,Joseph Muenzer,Barbara K. Burton,Can Ficicioglu,Heather A. Lau,Nancy D. Leslie,Edward Conner,Cheryl Wong Po Foo,Sagar A. Vaidya,Thomas Wechsler,Chester B. WhitleyMolecular Genetics and Metabolism(2018)引用 0|浏览1暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要