Nme 2 Cas9-mediated therapeutic editing in inhibiting angiogenesis after wet age-related macular degeneration onset.
Clinical and translational medicine(2023)
摘要
This study provides proof-of-concept possibility of employing Nme Cas9 for potential anti-angiogenesis therapy in wet AMD.
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关键词
choroidal neovascularization,gene editing,gene therapy,Nme2Cas9,wet AMD
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