HTA9 Evidence Generation Strategy and Insights for Rare Diseases: Case Studies of Mistakes Identified By NICE in Highly Specialized Technology (HST) Assessments

S. Aggarwal,S. Kumar, J. Topaloglu, A. Bela,O. Topaloglu

Value in Health(2023)

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摘要
To develop evidence generation strategic insights and lessons for ultra orphan drugs based on mistakes identified by NICE during Highly Specialized Technology (HST) assessments.
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关键词
hst,rare diseases,case studies,evidence
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