The vital role of natural history studies in rare disease: insights from X-linked dystonia parkinsonism.

Brain communications(2023)

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摘要
This scientific commentary refers to 'Establishing a natural history of X-linked dystonia parkinsonism', by Acuna et al. (https://doi.org/10.1093/braincomms/fcad106).
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关键词
dystonia parkinsonism,rare disease,natural history,natural history studies,x-linked
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