Gene Editing/Gene Therapies: PRECLINICAL EXPLORATION OF NOVEL ROUTES OF ADMINISTRATION FOR AN ADENO-ASSOCIATED VIRUS-BASED GENE THERAPY FOR THE TREATMENT OF LIPOPROTEIN LIPASE DEFICIENCY

N. Mehta, R. Gilbert,P. Chahal, M. Moreno, N. Nassoury, N. Coulombe, V. Lytvyn, M. Mercier, D. Fatehi,W. Lin, E. Harvey, L. Zhang, N. Nazemi-Moghaddam, S. Elahi,C. Ross,D. Stanimirovic,M. Hayden

Cytotherapy(2023)

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关键词
gene therapy,gene therapies,lipoprotein lipase,adeno-associated,virus-based
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