The Impact of Donidalorsen Taken Every 8 Weeks in Patients With Hereditary Angioedema

Journal of Allergy and Clinical Immunology(2023)

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摘要
To evaluate the effect of donidalorsen, an antisense inhibitor of prekallikrein (PKK), taken every 8 weeks in patients with hereditary angioedema (HAE), a disease characterized by recurrent, disabling swellings.
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donidalorsen
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