Risdiplam for the treatment of adults with spinal muscular atrophy: Experience of the Northern Ireland neuromuscular service

Gavin McCluskey, Siobhan Lamb, Sarah Mason, Grainne NicFhirleinn, Isobel Douglas,Sandya Tirupathi,Karen E. Morrison,John McConville

Muscle & Nerve(2022)

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关键词
spinal muscular atrophy,neuromuscular service,risdiplam
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