A High-Fidelity RNA-targeting Cas13 Restores Paternal Ube3a Expression and Improves Motor Functions in Angelman Syndrome Mice
MOLECULAR THERAPY(2023)
关键词
Angelman syndrome,RNA editing,high-fidelity Cas13,paternal Ube3a,motor function
AI 理解论文
溯源树
样例

生成溯源树,研究论文发展脉络
Chat Paper
正在生成论文摘要