Update on AAVance, a Phase 2/3 Clinical Trial of LYS-SAF302 Gene Therapy in Children with MPS IIIA R. Laufer, K. Aiach, A. Chakrapani, R. G. Crystal, M. Deneux, P. Drevot, L. Emrick, L. Giersch, B. Heron,M. Hocquemiller,N. Muschol, T. Kariyawasam, X. Mei, S. Saintpierre, M. Trad,R. Wang,C. B. Whitley, F. A. WijburgHUMAN GENE THERAPY(2022)引用 0|浏览6暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要