Tafamidis concentration required for transthyretin stabilisation in cerebrospinal fluid.
Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis(2023)
摘要
Tafamidis stabilises TTR in CSF to what is likely a clinically meaningful extent at CSF concentrations achieved by the normal tafamidis dosing regimen.
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关键词
Amyloid,CNS amyloidosis,kinetic stabilisation,tafamidis,transthyretin
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