Neurofilament light as a biomarker for involvement of the brain in classic infantile Pompe patients

M. Mackenbach, J. van den Dorpel,N. van der Beek, E. Willemse,D. Rizopoulos,C. Teunissen,A. van der Ploeg,J. van den Hout

NEUROMUSCULAR DISORDERS(2022)

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