EFFICIENT CORRECTION HUTCHINSON-GILFORD PROGERIA SYNDROME MUTATION IN IPSC USING ADENINE BASE EDITING

K.D. Asensi, K.P.M. Rodrigues,G.F. Castro,A.F. de Figueiredo, D.B.P. Campos, J.P. Pereira, T.H. Kasai-Brunswick,A.C. Campo de Carvalho

Cytotherapy(2022)

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关键词
Adenine base editors,Induced pluripotent stem cells,Hutchinson-Gilford progeria syndrome
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