594 Correction of a cystic fibrosis transmembrane conductance regulator canonical splice site variant, 3120+1G >A, by adenine base editing

A. Joynt,E. Kavanagh, S. Mitchell,G. Newby, D. Liu,N. Sharma, G. Cutting

Journal of Cystic Fibrosis(2022)

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adenine base editing
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