HUMAN IPSC-DERIVED ORGANOID MODEL RECAPITULATES RESCUABLE KEY PATHOLOGY FEATURES OF CMT1A

JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM(2022)

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关键词
Charcot-Marie-Tooth neuropathy, iPSC-derived organoid cultures, Myelinating Schwann cells, Short-hairpin RNAs targeting PMP22, PXT3003
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