Fenfluramine treatment for dravet syndrome: Real-world benefits on quality of life from the caregiver perspective

Epilepsy Research(2022)

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摘要
•Caregivers of Dravet syndrome patients report many fenfluramine treatment benefits.•Both seizure-related and quality of life benefits in patients are reported.•Caregivers also report improvements in their own quality of life.
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DS,FFA,QOL,REDCap
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