Base Editing of a gamma-Globin cis-Regulatory Elementin Human Hematopoietic Stem Cells for Reactivation of Therapeutic Fetal HemoglobinPanagiotis Antoniou,Giulia Hardouin,Pierre Martinucci,Giacomo Frati,Tristan Felix,Anne Chalumeau, Letizia Fontana,Megane Brusson,Giulia Maule,Jean-Paul Concordet,Mario Amendola,Marina Cavazzana,Anna Cereseto,Oriana Romano,Annarita MiccioMOLECULAR THERAPY(2022)引用 0|浏览3暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要