Optimization of Pre-mRNA Exon Editing for Efficient Rescue of Protein Expression
Kirk B. Burkhart,Kelly Becker,Rebekka Krumbach,John Bachmann,Bennett Bremer,Eric Carlin,Adam Clemens,Tayla Cormier,Conor Delaney,Akiko Doi,Lai Mung Fong,Kirk Gosik,Yevgenia Khodor,Xiaojin Liu,Savita Matapurkar,Julia Meredith,Akiko Noma,Anika Pavis,Lingtao Peng,Madison Stulir,Dennis Wu,Qin Yu, Laura Barrio Real,Scott Dooley,Gabrielle Hillman, Krishna Jawaharial, Linda Liu,Bruce C. Schnepp, Jasmine Shong,Philip R. Johnson,Robert D. Bell,Carrie Wager, Crystal S. Byers,Shimyn Slomovic,Jesse Gray,Michael D. Ehlers MOLECULAR THERAPY(2022)
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