Development of an AAV-Based microRNA Gene Therapy for Myotonic Dystrophy Type 1Giulio Srubek Tomassy,Wei Fan, Alessandro Magli, Tracy Zhang, Kristen Boyle,James Cao,Robert Jackson,Jennifer Sullivan,Amy M. Frederick,Catherine O'Riordan,Martin Goulet,Christian MuellerMOLECULAR THERAPY(2023)引用 0|浏览10暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要