An AAV9 Encoding Human ABCD1 (SBT101) Shows Functional Improvement Following Spinal Cord Delivery in a Rodent Model of AdrenomyeloneuropathyA. Pujol,A. Bosch,I. M. E. Dijkstra,S. Kemp,Y. R. J. Jaspers, S. Verdes, S. Fourcade, C. Guilera, M. Leal-Julia, A. Onieva, V. Vasireddy, S. W. Clark, D. W. Anderson,K. KozarskyMOLECULAR THERAPY(2022)引用 0|浏览6暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要