Farber disease clinical impact: Patient reported outcomes as a measure of disease burden
John Mitchell,Paul Harmatz,Laila Selim,Iman Gamal El Din,Neslihan Mungan,Fatma Bulut,Christina Lampe,Christina L. Grant,Carlos R. Ferreira,Ratna D. Puri,Sunita Bijarnia-Mahay,Nur Arslan,Norberto Guelbert,Maha S. Zaki,Seema Kapoor,Andreas Hahn,Bo Magnusson,Erik Sundberg,Seza Ozen,Ezgi D. Batu,Maja Di Rocco,Gulden Gokcay,Kathleen Crosby,Alexander Solyom MOLECULAR GENETICS AND METABOLISM(2022)
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