JAK-inhibition in a Patient with a STAT1 Gain-of-function Variant Reveals STAT1 Dysregulation As a Common Feature of Aplastic Anemia
Med(2022)
关键词
Aplastic anemia,autoimmune,STAT1 GOF,STAT1 gain-of-function,itacitinib,JAK inhibition,JAK/STAT,T-cell exhaustion,interferon gamma
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