Long-term multisystemic efficacy with migalastat in ERT-naive and ERT-experienced patients with amenable GLA variantsRobert J. Hopkin,Daniel G. Bichet,Gere Sunder-Plassmann,Kathleen Nicholls,Iacopo Olivotto,Roberto Giugliani,Eva Krusinska,Biliana Veleva-Rotse,Derralynn HughesMolecular Genetics and Metabolism(2022)引用 0|浏览4暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要