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Oligonucleotide Correction of an Intronic TIMMDC1 Variant in Cells of Patients with Severe Neurodegenerative Disorder

npj Genomic Medicine(2022)

引用 10|浏览28
关键词
Clinical genetics,Molecular medicine,Biomedicine,general,Human Genetics,Internal Medicine,Bioinformatics,Gene Therapy,Gene Function
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