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CRISPR/Cas9 Editing of Directly Reprogrammed Myogenic Progenitors Restores Dystrophin Expression in a Mouse Model of Muscular Dystrophy

Stem Cell Reports(2022)

引用 11|浏览16
关键词
direct lineage reprogramming,CRISPR/Cas9 editing of myogenic stem cells,Duchenne muscular dystrophy,stem-cell-based therapy
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