LGMD: EP.185 Safety -sarcoglycan expression, and functional outcomes from systemic gene transfer of rAAVrh74.MHCK7.hSGCB in LGMD2E/R4L. Rodino-Klapac, E. Pozsgai,S. Lewis,D. Griffin,A. Meadows,K. Lehman,K. Church, N. Reash,M. Iammarino,L. Lowes,E. Koenig,S. Neuhaus,X. Li,J. MendellNeuromuscular Disorders(2021)引用 0|浏览1暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要