The First Real-World Experience with Betibeglogene Autotemcel (beti-cel) Gene Therapy Treatment for Transfusion-Dependent β-Thalassemia (TDT)

Joachim B. Kunz, Eva Roth, Adil Mirza, Johann Greil,Petra Pavel,Anita Schmitt,Michael Schmitt, Alexander Kunz,Andreas E. Kulozik

Blood(2021)

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betibeglogene autotemcel,betibeglogene therapy treatment,real-world,beti-cel,transfusion-dependent
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